PMID-35368070 – Long-term Safety of Growth Hormone in 15809 Adults

PMID-35368070 – Long-term Safety of Growth Hormone in 15,809 Adults

Johannsson G et al. "Safety of Growth Hormone Replacement in Adults With Growth Hormone Deficiency: Results From a Large Observational Study," Journal of Clinical Endocrinology & Metabolism, 2022;107(8):e3198-e3209. doi:10.1210/clinem/dgac199

Quick Reference

Property Value
PMID 35368070
DOI 10.1210/clinem/dgac199
Year 2022
Journal Journal of Clinical Endocrinology & Metabolism
Study Type Observational (prospective registry)
Evidence Level III
Sample n=15,809 GH-treated adults
Peptide(s) Studied GH-axis peptides (exogenous GH therapy as proxy)

Key Findings

  • REASSURING: Cancer standardized incidence ratio (SIR) of 0.92 in GH-treated adults — comparable to the general population
  • No increased risk of de novo malignancy with long-term GH replacement therapy
  • No increased recurrence risk in patients with history of prior malignancy
  • Results consistent across age groups, sex, and GH deficiency etiology
  • Long follow-up duration strengthens the safety signal
  • This is the largest safety dataset for GH replacement therapy in adults to date

Study Design

Prospective observational registry study (KIMS — Pfizer International Metabolic Database) tracking 15,809 adults with GH deficiency receiving GH replacement therapy. Cancer incidence compared to age- and sex-matched general population rates using standardized incidence ratios. Extended follow-up period of up to 20 years for some patients.

Limitations

  • Observational design; no randomized control group
  • Registry data may be subject to ascertainment bias (closer monitoring in GH-treated patients)
  • GH doses used in replacement therapy may differ from doses achieved by GH-secretagogue peptides
  • Industry-sponsored registry (Pfizer)
  • Healthy user effect possible — patients deemed too high-risk may not have been enrolled

Clinical Relevance

This is the key reassurance study for GH-axis peptide prescribing. With 15,809 patients and up to 20 years of follow-up, the SIR of 0.92 provides strong evidence that physiological GH replacement does not increase cancer risk. This directly counters the alarming signal from Deodati 2014 (PMID-24818783) by using a much larger, better-controlled cohort. For practitioners using CJC-1295, Ipamorelin, Tesamorelin, or other GH-axis peptides, this study supports safety when IGF-1 is monitored within physiological ranges.

Related

#research #observational #evidence-level-III #cancer